Neuren Pharmaceuticals Limited
Company Overview: Neuren Pharmaceuticals Limited is a biopharmaceutical company specializing in the development of drugs for neurological disorders. Founded in 2001 and headquartered in Camberwell, Australia, the company focuses on innovative treatments for rare and complex neurological conditions.
Key Developments & Pipeline
- DAYBUE (trofinetide): Approved for the treatment of Rett syndrome in adults and pediatric patients aged 2 years and older. Currently in Phase 2 clinical trials for Fragile X syndrome.
- NNZ-2591:
- Completed Phase 2 trials for Phelan-McDermid syndrome.
- In Phase 2 trials for Angelman syndrome and Pitt Hopkins syndrome.
- In preclinical development for Prader-Willi syndrome.